Securing & Maintaining Access & Reimbursement for Rare Disease Therapies
Apr 8, 2025
Rare diseases, impacting fewer than 200,000 individuals in the US, present daunting access and reimbursement obstacles, with 95% lacking approved therapy. As the median treatment cost exceeds $200,000 annually, concerns about affordability, access, and value persist for over 10,000 identified rare diseases, affecting 30 million Americans.